Publication | Open Access
A novel gene editing system to treat both Tay–Sachs and Sandhoff diseases
53
Citations
47
References
2020
Year
Gene TherapiesNovel GeneIn Vivo Gene TherapyGenome SurgeryNatural SciencesGeneticsPathogenesisNovel TherapySandhoff DiseasesGenetic EngineeringPathologyGene EditingGenome EngineeringGene VectorGene ExpressionMedicineGenome Editing
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