S. Hacein-Bey-Abina

<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1

S. Hacein-Bey-Abina, Christof von Kalle, Manfred Schmidt et al. · Science · 2003 · 3.6K citations

Life Sciences, Genetics, Immunology +17

Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott–Aldrich syndrome

Alessandra Magnani, Michaëla Semeraro, Frédéric Adam et al. · Nature Medicine · 2022 · 118 citations · Full text

Medicine, Hematology, Immunology +17

Fragile sites are preferential targets for integrations of MLV vectors in gene therapy

Assaf C. Bester, Michal Schwartz, Manfred Schmidt et al. · Gene Therapy · 2006 · 51 citations

Life Sciences, Genetics, Molecular Biology +12

Critical Variables affecting clinical-grade production of the self-inactivating gamma-retroviral vector for the treatment of X-linked severe combined immunodeficiency

Johannes C.M. van der Loo, William Swaney, Elke Grassman et al. · Gene Therapy · 2012 · 14 citations · Full text

Life Sciences, Immunology, Clinical Immunology +14