Concepedia

Publication | Open Access

A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome

DOIFull Paper Access

58

Citations

53

References

2016

Year

Giuseppe Ronzitti, Giulia Bortolussi, Remco van Dijk, Fanny Collaud, Séverine Charles, Christian Leborgne, Patrice Vidal, Samia Martin, Bernard Gjata, Marcelo Simon Sola,
Molecular Therapy — Methods & Clinical Development

References

YearCitations

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