Concepedia

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

Catherine S. Manno, Glenn F. Pierce, Valder R. Arruda, Bertil Glader, Margaret V. Ragni, John E.J. Rasko, Margareth C. Ozelo, Keith Hoots, Philip M. Blatt, Barbara A. Konkle,

Nature Medicine · 2006 · 2.1K citations · 27 references

DOI

Concepts

References

27

An Algorithm for the Grading of Activity in Chronic Hepatitis C

Pierre Bédossa, Thierry Poynard · Hepatology · 1996 · 4K citations · Full text

, , +17

Intraobserver and Interobserver Variations in Liver Biopsy Interpretation in Patients With Chronic Hepatitis C

Pierre Bédossa · Hepatology · 1994 · 2K citations · Full text

, , +16

Gene therapy restores vision in a canine model of childhood blindness

Gregory M. Acland, Jharna Ray, Qí Zhāng et al. · Nature Genetics · 2001 · 1.2K citations

, , +16

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector

Mark A. Kay, Catherine S. Manno, Margaret V. Ragni et al. · Nature Genetics · 2000 · 1K citations

, , +14

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B

Catherine S. Manno, Ah Keng Chew, S Hutchison et al. · Blood · 2003 · 747 citations · Full text

, , +11