John E.J. Rasko

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

Catherine S. Manno, Glenn F. Pierce, Valder R. Arruda et al. · Nature Medicine · 2006 · 2.1K citations

Life Sciences, Hematology, Molecular Genetics +9

Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant

Lindsey A. George, Spencer K. Sullivan, Adam Giermasz et al. · New England Journal of Medicine · 2017 · 759 citations · Full text

Medicine, Hematology, Molecular Medicine +15

CD8+ T-cell responses to adeno-associated virus capsid in humans

Federico Mingozzi, Marcela V. Maus, Daniel J. Hui et al. · Nature Medicine · 2007 · 726 citations

Life Sciences, Immunology, Infectious Diseases +14

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2018 · 661 citations · Full text

Medicine, Genetics, Hematology +16

ASCT2/SLC1A5 controls glutamine uptake and tumour growth in triple-negative basal-like breast cancer

Michelle van Geldermalsen, Qian Wang, Rajini Nagarajah et al. · Oncogene · 2015 · 585 citations · Full text

Medicine, Oncology, Pharmacology +14