Daniel J. Hui

Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant

Lindsey A. George, Spencer K. Sullivan, Adam Giermasz et al. · New England Journal of Medicine · 2017 · 759 citations · Full text

Medicine, Hematology, Molecular Medicine +15

CD8+ T-cell responses to adeno-associated virus capsid in humans

Federico Mingozzi, Marcela V. Maus, Daniel J. Hui et al. · Nature Medicine · 2007 · 726 citations

Life Sciences, Immunology, Infectious Diseases +14

Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys

Federico Mingozzi, Xavier M. Anguela, Giulia Pavani et al. · Science Translational Medicine · 2013 · 344 citations · Full text

Life Sciences, Immunology, Molecular Medicine +14

AAV-1–mediated gene transfer to skeletal muscle in humans results in dose-dependent activation of capsid-specific T cells

Federico Mingozzi, J. J. M. Meulenberg, Daniel J. Hui et al. · Blood · 2009 · 284 citations · Full text

Life Sciences, Immunology, Molecular Biology +13

Reversal of Blindness in Animal Models of Leber Congenital Amaurosis Using Optimized AAV2-mediated Gene Transfer

Jeannette Bennicelli, J. Fraser Wright, András M. Komáromy et al. · Molecular Therapy · 2008 · 268 citations · Full text

Medicine, Ophthalmology, Vision Science +17