Concepedia

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector

Mark A. Kay, Catherine S. Manno, Margaret V. Ragni, Peter J. Larson, Linda B. Couto, Alan McClelland, Bertil Glader, Shing Jen Tai, Roland W. Herzog, Valder R. Arruda,

Nature Genetics · 2000 · 1K citations · 15 references

DOI

Concepts

References

15

Membrane-Associated Heparan Sulfate Proteoglycan Is a Receptor for Adeno-Associated Virus Type 2 Virions

Candace Summerford, R. Jude Samulski · Journal of Virology · 1998 · 1.4K citations · Full text

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Complete nucleotide sequences of the gene for human factor IX (antihemophilic factor B)

Shinji Yoshitake, Barbara G. Schach, Donald C. Foster et al. · Biochemistry · 1985 · 667 citations

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Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

Roland W. Herzog, Edmund Y. Yang, Linda B. Couto et al. · Nature Medicine · 1999 · 562 citations

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Adeno-associated virus vectors can be efficiently produced without helper virus

Takashi Matsushita, SS Elliger, CA Elliger et al. · Gene Therapy · 1998 · 495 citations

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Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

Roland W. Herzog, J. Nathan Hagstrom, Szu-Hoo Kung et al. · Proceedings of the National Academy of Sciences · 1997 · 474 citations

, , +17