Concepedia
Statistics
Publications
24
Citations
1.4K
H-Index
20
Active since
1994
Affiliations
Genethon (France)(Current)
Inserm
Sorbonne Université
Université Paris-Saclay
Centre de Recherche en Myologie
Bernard Gjata is an author at Genethon (France) specializing in gene therapy, immunology, and gene delivery.
Publications per year
1994–2021
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
Caroline Le Guiner, Laurent Servais, Marie Montus et al. · Nature Communications · 2017 · 233 citations · Full text
Medicine, Molecular Medicine, Veterinary Clinical Sciences +17
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase
Francesco Puzzo, Pasqualina Colella, Maria Grazia Biferi et al. · Science Translational Medicine · 2017 · 133 citations
Pharmacy, Biochemistry, Biotechnology +11
Successful Interference with Cellular Immune Responses to Immunogenic Proteins Encoded by Recombinant Viral Vectors
Adélaïda Sarukhan, Sabine Camugli, Bernard Gjata et al. · Journal of Virology · 2001 · 117 citations · Full text
Life Sciences, Immunology, Cellular Immunology +12
A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C
Serge Herson, Fayçal Hentati, Aude Rigolet et al. · Brain · 2011 · 87 citations
Medicine, Genetics, Molecular Medicine +14
Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott–Aldrich Syndrome in Preclinical Models
Francesco Marangoni, Marita Bosticardo, Sabine Charrier et al. · Molecular Therapy · 2009 · 84 citations · Full text
Life Sciences, Hematology, Immunology +17
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