Insertional Transformation of Hematopoietic Cells by Self-inactivating Lentiviral and Gammaretroviral Vectors

Ute Modlich, Susana Navarro, Daniela Zychlinski, +9

Molecular Therapy

Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome

Salima Hacein-Bey Abina, H. Bobby Gaspar, Johanna Blondeau, +29

JAMA

NK cell activation by dendritic cells (DCs) requires the formation of a synapse leading to IL-12 polarization in DCs

Christophe Borg, Abdelali Jalil, Diego J. Laderach, +10

Blood

Large-Scale Manufacture and Characterization of a Lentiviral Vector Produced for Clinical <i>Ex Vivo</i> Gene Therapy Application

Otto-Wilhelm Merten, Sabine Charrier, Nicolas Laroudie, +11

Human Gene Therapy

Germline duplication of ATG2B and GSKIP predisposes to familial myeloid malignancies

Joseph Saliba, Cécile Saint‐Martin, Antonio Di Stefano, +28

Nature Genetics

Hematological MalignancySomatic VariantGeneticsMalignant Blood DisorderPathology +5

Clinical and pathological response to primary chemotherapy in operable breast cancer

P. Chollet, Sabine Charrier, Étienne Brain, +7

European Journal of Cancer

Surgical OncologyBreast OncologyMedicinePathologyPathological Response +6

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients

Sabine Charrier, Loı̈c Dupré, Samantha Scaramuzza, +9

Gene Therapy

Cell TherapyWas PatientsWasp ExpressionImmunologyLentiviral Vectors +4

High-Dose Plasma Infusion versus Plasma Exchange as Early Treatment of Thrombotic Thrombocytopenic Purpura/Hemolytic-Uremic Syndrome

Paul Coppo, A Bussel, Sabine Charrier, +9

Medicine

A lentiviral vector encoding the human Wiskott–Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice

Sabine Charrier, Daniel Stockholm, Khalil Seye, +8

Gene Therapy

ImmunogeneticsCytoskeletal DefectsImmune Cell DevelopmentImmunodeficienciesPathogenesis +13

Technetium-99m-sestamibi uptake in breast tumor and associated lymph nodes.

J. Maublant, M de Latour, D. Mestas, +7

PubMed