Concepedia

Phase 2 gene therapy trial of an anti-HIV ribozyme in autologous CD34+ cells

Ronald T. Mitsuyasu, Thomas C. Merigan, Andrew Carr, Jerome A. Zack, Mark A. Winters, Cassy Workman, Mark Bloch, Jacob Lalezari, S. Hegewisch Becker, Lorna Thornton,

Nature Medicine · 2009 · 263 citations · 33 references

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33

<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1

S. Hacein-Bey-Abina, Christof von Kalle, Manfred Schmidt et al. · Science · 2003 · 3.6K citations

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CD4+ Count–Guided Interruption of Antiretroviral Treatment

New England Journal of Medicine · 2006 · 2.2K citations · Full text

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Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1

Marion Ott, Manfred Schmidt, Kerstin Schwarzwaelder et al. · Nature Medicine · 2006 · 1.2K citations

, , +10

Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning

Alessandro Aiuti, Shimon Slavin, Memet Aker et al. · Science · 2002 · 1.1K citations

, , +15

Ribozymes as Potential Anti-HIV-1 Therapeutic Agents

Nava Sarver, Edouard M. Cantin, Pairoj S. Chang et al. · Science · 1990 · 663 citations

, , +15