Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls
Suzanne Kroes,
Marlou C. Bierlaagh,
Juliet Lefferts,
Alessandra Boni,
Danya Muilwijk,
C. Viscomi,
Natascha D A Keijzer-Nieuwenhuijze,
Luca Cristiani,
Paul J Niemöller,
Tibo F. Verburg,
Journal of Cystic Fibrosis · 2024 · 11 citations · 23 references