Nature Biotechnology · 2024 · 86 citations · 36 references
Life SciencesGeneticsMolecular BiologyGene TherapyGenome EditingSynthetic BiologyCrispr-based EngineeringCrispr-cas SystemsGuide Rna DesignPrime EditingRna EditingTherapeutic Genome EditingCircular RnasCrispr-cas Genome EditingHuman Embryonic Stem CellsIn Vivo Genome EditingSingle-guide Rna Design
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A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity
Martin Jínek, Krzysztof Chylinski, Ines Fonfara et al. · Science · 2012 · 17.3K citations · Full text
Cpf1 Is a Single RNA-Guided Endonuclease of a Class 2 CRISPR-Cas System
Bernd Zetsche, Jonathan S. Gootenberg, Omar O. Abudayyeh et al. · Cell · 2015 · 4.9K citations · Full text
Search-and-replace genome editing without double-strand breaks or donor DNA
Andrew V. Anzalone, Peyton B. Randolph, Jessie R. Davis et al. · Nature · 2019 · 4.7K citations · Full text
Crystal Structure of Cas9 in Complex with Guide RNA and Target DNA
Hiroshi Nishimasu, F. Ann Ran, Patrick D. Hsu et al. · Cell · 2014 · 2.4K citations · Full text