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Toxicity after AAV delivery of RNAi expression constructs into nonhuman primate brain

Megan S. Keiser, Paul T. Ranum, Carolyn M. Yrigollen, Ellie M. Carrell, Geary R. Smith, Amy Muehlmatt, Yong Hong Chen, Joel M. Stein, Ronald L. Wolf, Enrico Radaelli,

Nature Medicine · 2021 · 73 citations · 29 references

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29

Moderated estimation of fold change and dispersion for RNA-seq data with DESeq2

Michael I. Love, Wolfgang Huber, Simon Anders · Genome biology · 2014 · 100.5K citations · Full text

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STAR: ultrafast universal RNA-seq aligner

Alexander Dobin, Carrie Davis, Felix Schlesinger et al. · Bioinformatics · 2012 · 56.2K citations · Full text

, , +17

Minimap2: pairwise alignment for nucleotide sequences

Heng Li · Bioinformatics · 2018 · 16.8K citations · Full text

, , +17

Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial

Albert M. Maguire, Katherine A. High, Alberto Auricchio et al. · The Lancet · 2009 · 858 citations

, , +12

RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia

Haibin Xia, Qinwen Mao, Steven Eliason et al. · Nature Medicine · 2004 · 651 citations

, , +14