Publication | Closed Access
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial
849
Citations
25
References
2009
Year
Gene TherapiesGenetic DisorderGeneticsClinical TrialsTranslational ResearchCongenital AmaurosisPhase 1MedicineRpe65 Gene TherapyNovel Therapy
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