Settimio Rossi

Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis

Albert M. Maguire, Francesca Simonelli, Eric A. Pierce et al. · New England Journal of Medicine · 2008 · 2.1K citations · Full text

Medicine, Genetics, Ophthalmology +17

Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial

Albert M. Maguire, Katherine A. High, Alberto Auricchio et al. · The Lancet · 2009 · 858 citations

Medicine, Genetics, Molecular Genetics +12

Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration

Francesca Simonelli, Albert M. Maguire, Francesco Testa et al. · Molecular Therapy · 2009 · 551 citations · Full text

Medicine, Immunology, Ophthalmology +15

Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2

Francesco Testa, Albert M. Maguire, Settimio Rossi et al. · Ophthalmology · 2013 · 329 citations · Full text

Veterinary Medicine, Infectious Diseases, Surgery +6

Effective delivery of large genes to the retina by dual AAV vectors

Ivana Trapani, Pasqualina Colella, Andrea Sommella et al. · EMBO Molecular Medicine · 2013 · 262 citations · Full text

Medicine, Biotechnology, Ophthalmology +17