Concepedia

In vivo genome editing of mucopolysaccharidosis I mice using the CRISPR/Cas9 system

Roselena Silvestri Schuh, Édina Poletto, Gabriela Pasqualim, Ângela Maria Vicente Tavares, Fabíola Shons Meyer, Esteban Alberto Gonzalez, Roberto Giugliani, Úrsula da Silveira Matte, Hélder Ferreira Teixeira, Guilherme Baldo

Journal of Controlled Release · 2018 · 70 citations · 39 references

DOI

Concepts

References

39

A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity

Martin Jínek, Krzysztof Chylinski, Ines Fonfara et al. · Science · 2012 · 17.3K citations · Full text

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Multiplex Genome Engineering Using CRISPR/Cas Systems

Le Cong, F. Ann Ran, David Cox et al. · Science · 2013 · 15.7K citations

, , +16

RNA-Guided Human Genome Engineering via Cas9

Prashant Mali, Luhan Yang, Kevin M. Esvelt et al. · Science · 2013 · 9.4K citations · Full text

, , +15

One-Step Generation of Mice Carrying Mutations in Multiple Genes by CRISPR/Cas-Mediated Genome Engineering

Haoyi Wang, Hui Yang, Chikdu Shivalila et al. · Cell · 2013 · 3.6K citations · Full text

, , +14

High Levels of Foreign Gene Expression in Hepatocytes after Tail Vein Injections of Naked Plasmid DNA

G Zhang, Vladimir G. Budker, Jon A. Wolff · Human Gene Therapy · 1999 · 950 citations

, , +14