Publication | Closed Access
In vivo genome editing of mucopolysaccharidosis I mice using the CRISPR/Cas9 system
68
Citations
39
References
2018
Year
Knockout MouseOff-target EffectEngineeringGenome SurgeryIn Vivo Gene TherapyVivo Genome EditingImmunologyGenetic EngineeringSynthetic BiologyGene EditingGenome EngineeringCrisprCrispr/cas9 SystemMedicineCell BiologyGenome Editing
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