Concepedia

Validation of a mutated PRE sequence allowing high and sustained transgene expression while abrogating WHV-X protein synthesis: application to the gene therapy of WAS

Maria Antonietta Zanta-Boussif, Sabine Charrier, A Brice-Ouzet, Susan S. Martin, Paule Opolon, Adrian J. Thrasher, Thomas J. Hope, Anne Galy

Gene Therapy · 2009 · 86 citations · 27 references

DOI

Concepts

References

27

Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo

Romain Zufferey, Dea Nagy, Ron J. Mandel et al. · Nature Biotechnology · 1997 · 2K citations · Full text

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Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances Expression of Transgenes Delivered by Retroviral Vectors

Romain Zufferey, John E. Donello, Didier Trono et al. · Journal of Virology · 1999 · 1K citations · Full text

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Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

Eugenio Montini, Daniela Cesana, Manfred Schmidt et al. · Nature Biotechnology · 2006 · 705 citations

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Wiskott-Aldrich Syndrome Protein-Deficient Mice Reveal a Role for WASP in T but Not B Cell Activation

Scott B. Snapper, Fred S. Rosen, Emiko Mizoguchi et al. · Immunity · 1998 · 493 citations · Full text

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Woodchuck Hepatitis Virus Contains a Tripartite Posttranscriptional Regulatory Element

John E. Donello, Jonathan E. Loeb, Thomas J. Hope · Journal of Virology · 1998 · 356 citations · Full text

, , +17