Nature Biotechnology · 2024 · 56 citations · 27 references
Life SciencesGeneticsMolecular BiologyDna RepairGenome EditingGenome EngineeringCrispr-cas SystemsViral GeneticsCrispr-cas9-mediated RepairGenome Editing Via Viral VectorsPrecision Genome EngineeringViral Genome EditingViral Genome EngineeringViral Genome Integration SitesViral Vector IntegrationViral Vectors
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Isolation of Single Human Hematopoietic Stem Cells Capable of Long-Term Multilineage Engraftment
Faiyaz Notta, Sergei Doulatov, Elisa Laurenti et al. · Science · 2011 · 888 citations
CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells
Daniel P. Dever, Rasmus O. Bak, Andreas Reinisch et al. · Nature · 2016 · 876 citations · Full text
An inducible caspase 9 safety switch for T-cell therapy
Karin Straathof, Martin Pulé, Patricia Yotnda et al. · Blood · 2005 · 741 citations · Full text