Nature · 2016 · 876 citations · 35 references
Life SciencesGeneticsMolecular GeneticsGenome EditingGenomicsStem Cell BiologyCrispr-cas SystemsHematopoietic DevelopmentHematopoietic DifferentiationHematopoietic Stem Cell BiologyHematopoietic Stem CellsTherapeutic Genome EditingCrispr-based Genome EngineeringCrispr-cas9 Genome EditingCrispr-cas9 KnockoutHematopoietic Stem Cell EditingIn Vivo Genome Editing
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A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity
Martin Jínek, Krzysztof Chylinski, Ines Fonfara et al. · Science · 2012 · 17.3K citations · Full text
Easy quantitative assessment of genome editing by sequence trace decomposition
Eva K. Brinkman, Tao Chen, Mario Amendola et al. · Nucleic Acids Research · 2014 · 2.6K citations · Full text
Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
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HSV-TK Gene Transfer into Donor Lymphocytes for Control of Allogeneic Graft-Versus-Leukemia
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Medicine, Hematology, Immunology +7