Publication | Closed Access
Correction of a CADASIL point mutation using adenine base editors in hiPSCs and blood vessel organoids
18
Citations
37
References
2023
Year
Blood Vessel OrganoidsCadasil Point MutationSomatic VariantIn Vivo Gene TherapyMedicinePathologyAdenine Base EditorsMolecular DiagnosticsRadiation OncologyGenome EditingVariant InterpretationMutagenesis
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