Molecular Therapy · 2018 · 131 citations · 52 references
Life SciencesBiotechnologyMolecular BiologyGene DeliveryGenome EditingVirologyCrispr-cas SystemsGene Delivery VectorsGene Editing Payload DeliveryProtein DeliveryVector ProductionCrispr-cas9 Genome EditingDelivery Systems For CrisprEx Vivo DeliveryExtracellular Vesicle TherapyGuide Rna-directed EditingTransient Gene TransferViral Vector DeliveryVirally Derived Delivery Vectors
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DNA targeting specificity of RNA-guided Cas9 nucleases
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Delivery of siRNA to the mouse brain by systemic injection of targeted exosomes
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High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells
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Easy quantitative assessment of genome editing by sequence trace decomposition
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