Concepedia

CRISPR-Cas9-mediated gene editing in human MPS I fibroblasts

Talita Giacomet de Carvalho, Roselena Silvestri Schuh, Gabriela Pasqualim, Felipe Mateus Pellenz, Eduardo Cremonese Filippi‐Chiela, Roberto Giugliani, Guilherme Baldo, Úrsula da Silveira Matte

Gene · 2018 · 23 citations · 14 references

DOI

Concepts

References

14

Prevention of muscular dystrophy in mice by CRISPR/Cas9–mediated editing of germline DNA

Chengzu Long, John McAnally, John M. Shelton et al. · Science · 2014 · 721 citations · Full text

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Correction of a Genetic Disease in Mouse via Use of CRISPR-Cas9

Yuxuan Wu, Dan Liang, Yinghua Wang et al. · Cell stem cell · 2013 · 612 citations · Full text

, , +11

Targeted genome editing in human repopulating haematopoietic stem cells

Pietro Genovese, Giulia Schiroli, Giulia Escobar et al. · Nature · 2014 · 565 citations · Full text

, , +14

Seamless gene correction of β-thalassemia mutations in patient-specific iPSCs using CRISPR/Cas9 and <i>piggyBac</i>

Fei Xie, Lin Ye, Judy C. Chang et al. · Genome Research · 2014 · 406 citations · Full text

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Ratiometric analysis of Acridine Orange staining in the study of acidic organelles and autophagy

Marcos Paulo Machado Thomé, Eduardo Cremonese Filippi‐Chiela, Emilly S. Villodre et al. · Journal of Cell Science · 2016 · 305 citations · Full text

, , +15