Experimental Eye Research · 2018 · 13 citations · 39 references
MedicineMolecular BiologyMolecular GeneticsDna RepairGenome EditingOcular GeneticsCrispr-based EngineeringCrispr-cas SystemsInner Retinal FunctionOcular Gene TherapyRetinal DevelopmentRetinal NeurobiologyCrispr-based Genome EngineeringCrispr-cas9 Genome EditingCrispr-cas9 KnockoutCrispr-cas9 Knockout ModelsCrispr-cas9 Mediated Knock-inEssential Gene FunctionRetinal Disease Models
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A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity
Martin Jínek, Krzysztof Chylinski, Ines Fonfara et al. · Science · 2012 · 17.3K citations · Full text
Multiplex Genome Engineering Using CRISPR/Cas Systems
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RNA-Guided Human Genome Engineering via Cas9
Prashant Mali, Luhan Yang, Kevin M. Esvelt et al. · Science · 2013 · 9.4K citations · Full text
Repurposing CRISPR as an RNA-Guided Platform for Sequence-Specific Control of Gene Expression
Lei S. Qi, Matthew H. Larson, Luke A. Gilbert et al. · Cell · 2013 · 5.2K citations · Full text
In vivo genome editing using Staphylococcus aureus Cas9
F. Ann Ran, Le Cong, Winston X. Yan et al. · Nature · 2015 · 2.7K citations · Full text