Publication | Open Access
Allele-specific silencing of mutant huntingtin and ataxin-3 genes by targeting expanded CAG repeats in mRNAs
239
Citations
25
References
2009
Year
Cag RepeatsAllele-specific SilencingGeneticsGenomic MechanismGene RegulationMolecular GeneticsGene FunctionGene ExpressionMedicineCell BiologyRna ProcessingTranscription RegulationMutant Huntingtin
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