Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa

Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector

Xiao Xiao, Jing Li, R. Jude Samulski · Journal of Virology · 1996 · 911 citations · Full text

Life Sciences, Biotechnology, Molecular Biology +16

Photoreceptor degeneration in inherited retinal dystrophy delayed by basic fibroblast growth factor

Ella G. Faktorovich, Roy H. Steinberg, Douglas Yasumura et al. · Nature · 1990 · 717 citations

Medicine, Genetics, Ophthalmology +16

Recombinant adeno-associated virus for muscle directed gene therapy

Krishna J. Fisher, Karin Jooss, J. M. Alston et al. · Nature Medicine · 1997 · 654 citations

Medicine, Biotechnology, Molecular Genetics +11

A "humanized" green fluorescent protein cDNA adapted for high-level expression in mammalian cells

Sergei Zolotukhin, Mark Potter, William W. Hauswirth et al. · Journal of Virology · 1996 · 614 citations · Full text

Pharmacy, Biotechnology, Molecular Biology +17

Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector

Hiroyuki Miyoshi, Masayo Takahashi, Fred H. Gage et al. · Proceedings of the National Academy of Sciences · 1997 · 498 citations

Medicine, Neurobiology, Ophthalmology +12