Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1

Marion Ott, Manfred Schmidt, Kerstin Schwarzwaelder, +24

Nature Medicine

Gene TherapiesAutoimmune DiseaseNovel TherapyImmunodeficienciesImmunology +8

Genetic relationships determined by a DNA heteroduplex mobility assay: analysis of HIV-1 env genes

Eric Delwart, Eugene G. Shpaer, Joost Louwagie, +4

Science

GeneticsImmunologyGenetic EpidemiologyMolecular BiologyDna Analysis +21

Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

Stefan Stein, Marion Ott, Stephan Schultze‐Strasser, +25

Nature Medicine

Hematological MalignancyAutoimmune DiseaseGranulocyteEvi1 ActivationImmunology +10

High-Level Transduction and Gene Expression in Hematopoietic Repopulating Cells Using a Human Imunodeficiency Virus Type 1-Based Lentiviral Vector Containing an Internal Spleen Focus Forming Virus Promoter

Christophe Demaison, Kathryn L. Parsley, Gaby Brouns, +5

Human Gene Therapy

Hematopoietic Repopulating CellsViral ReplicationImmunologySpleen FocusImmunotherapy +15

5′-Terminal sequences of eucaryotic mRNA can be cloned with high efficiency

Hartmut Land, Manuel Grez, H. Häuser, +2

Nucleic Acids Research

Selective Inhibition of Tumor Growth by Clonal NK Cells Expressing an ErbB2/HER2-Specific Chimeric Antigen Receptor

Kurt Schönfeld, Christiane Sahm, Congcong Zhang, +18

Molecular Therapy

Exons encode functional and structural units of chicken lysozyme.

A. Jung, Albrecht E. Sippel, Manuel Grez, +1

Proceedings of the National Academy of Sciences

Protein ChemistryChicken LysozymeProtein ExpressionBiochemistryProtein Folding +11

Lentiviral gene therapy for X-linked chronic granulomatous disease

Donald B. Kohn, Claire Booth, Elizabeth M. Kang, +35

Nature Medicine

Primary ImmunodeficiencyAutoimmune DiseaseLentiviral Gene TherapyAutoimmunityDermatology +2

Deduced amino acid sequence from the bovine oxytocin–neurophysin I precursor cDNA

Hartmut Land, Manuel Grez, S Ruppert, +4

Nature

BiologyBiosynthesisMolecular PhysiologyBiochemistryNatural Sciences +8

Acetylation of Stat1 modulates NF-κB activity

Oliver H. Krämer, Daniela Baus, Shirley K. Knauer, +6

Genes & Development