Jonathan D. Finn

A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing

Jonathan D. Finn, Amy Smith, Mihir Patel et al. · Cell Reports · 2018 · 801 citations · Full text

In vivo genome editing restores haemostasis in a mouse model of haemophilia

Hojun Li, Virginia Haurigot, Yannick Doyon et al. · Nature · 2011 · 540 citations

Vivo Genome, Knockout Mouse, Engineering +12

X-Linked Thrombophilia with a Mutant Factor IX (Factor IX Padua)

Paolo Simioni, Daniela Tormene, Giulio Tognin et al. · New England Journal of Medicine · 2009 · 382 citations · Full text

Thrombopoiesis, Thrombosis, Factor Ix +12

A versatile platform for generating engineered extracellular vesicles with defined therapeutic properties

Kevin Dooley, Russell E. McConnell, Ke Xu et al. · Molecular Therapy · 2021 · 289 citations · Full text

Capsid antigen presentation flags human hepatocytes for destruction after transduction by adeno-associated viral vectors

Gary C. Pien, Etiena Basner‐Tschakarjan, Daniel J. Hui et al. · Journal of Clinical Investigation · 2009 · 188 citations · Full text

Adeno-associated Virus, Adeno-associated Viral Vectors, Viral Replication +14