Etiena Basner‐Tschakarjan

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

Amit C. Nathwani, Edward G. D. Tuddenham, Savita Rangarajan et al. · New England Journal of Medicine · 2011 · 1.8K citations · Full text

Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2014 · 1.2K citations · Full text

Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys

Federico Mingozzi, Xavier M. Anguela, Giulia Pavani et al. · Science Translational Medicine · 2013 · 335 citations · Full text

AAV-1–mediated gene transfer to skeletal muscle in humans results in dose-dependent activation of capsid-specific T cells

Federico Mingozzi, J. J. M. Meulenberg, Daniel J. Hui et al. · Blood · 2009 · 280 citations · Full text

Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver

Federico Mingozzi, Nicole C. Hasbrouck, Etiena Basner‐Tschakarjan et al. · Blood · 2007 · 245 citations · Full text