Annamaria Aprile

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese et al. · Nature Medicine · 2019 · 225 citations

Medicine, Hematology, Pediatrics +14

Bone marrow stromal cells from β-thalassemia patients have impaired hematopoietic supportive capacity

Stefania Crippa, Valeria Rossella, Annamaria Aprile et al. · Journal of Clinical Investigation · 2019 · 72 citations · Full text

Medicine, Cell Biology, Hematology +17

Plerixafor and G-CSF combination mobilizes hematopoietic stem and progenitors cells with a distinct transcriptional profile and a reduced <i>in vivo</i> homing capacity compared to plerixafor alone

Maria Rosa Lidonnici, Annamaria Aprile, Marta Claudia Frittoli et al. · Haematologica · 2016 · 41 citations · Full text

Life Sciences, Cell Biology, Hematology +16

Hematopoietic stem cell function in β-thalassemia is impaired and is rescued by targeting the bone marrow niche

Annamaria Aprile, Alessandro Gulino, Mariangela Storto et al. · Blood · 2020 · 35 citations · Full text

Life Sciences, Cell Biology, Hematology +14

Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia

Maria Rosa Lidonnici, Ylenia Paleari, Francesca Tiboni et al. · Molecular Therapy — Methods & Clinical Development · 2018 · 23 citations · Full text

Medicine, Biotechnology, Hematology +17