Maria Pia Cicalese

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Alessandra Biffi, Eugenio Montini, Laura Lorioli et al. · Science · 2013 · 1.2K citations · Full text

Life Sciences, Genetics, Hematology +16

Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome

Alessandro Aiuti, Luca Biasco, Samantha Scaramuzza et al. · Science · 2013 · 1K citations · Full text

Medicine, Cell Biology, Hematology +16

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial

Maria Sessa, Laura Lorioli, Francesca Fumagalli et al. · The Lancet · 2016 · 507 citations

Medicine, Hematology, Molecular Medicine +13

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora et al. · The Lancet · 2022 · 284 citations · Full text

Medicine, Hematology, Immunology +15

In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases

Luca Biasco, Danilo Pellin, Serena Scala et al. · Cell stem cell · 2016 · 241 citations · Full text

Life Sciences, Cell Biology, Hematology +17