Alessandra Biffi - Concepedia

Author

Alessandra Biffi

The San Raffaele Telethon Institute for Gene Therapy ORCID

Also Known As

A BIFFI, A Biffi, A. Biffi, Alessandra Biffi, Bernardo Maria, Biffi A, Biffi, A., Biffi, Alessandra, Paolo Biban, Parul Bhargava

271

Publications

10.7K

Citations

H-Index

164

Concepts

All Affiliations

The San Raffaele Telethon Institute for Gene Therapy Vita-Salute San Raffaele University University of Padua Dana-Farber/Boston Children's Cancer and Blood Disorders Center Istituti di Ricovero e Cura a Carattere Scientifico

About

Alessandra Biffi is an author at The San Raffaele Telethon Institute for Gene Therapy specializing in medicine, immunology, and cell biology.

Top Concepts

#	Concept	H-Index	Publications	Citations
1	Medicine	23	36	6.1K
2	Health Sciences	11	11	3.4K
3	Engineering	6	6	596
4	Education	3	3	55
5	Natural Sciences	2	2	230

Alessandra Biffi

Publications

9.4K

Citations

H-Index

Page 1

	Year	Citations
Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy Alessandra Biffi, Eugenio Montini, Laura Lorioli, Science Cell TherapyImmunologyBlood CellCell Replacement TherapyBone Marrow Failure	2013	1.2K
Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome Alessandro Aiuti, Luca Biasco, Samantha Scaramuzza, Science Cell TherapyLentiviral Gene TherapyImmunologyPathologyImmunotherapy	2013	1K
Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease Jin‐Kuk Kim, Chunguang Hu, Christelle Moufawad El Achkar, New England Journal of Medicine Genetic DiseasesNeurodegenerative DiseasesMiracle FoundationNeurological DisorderOligonucleotide	2019	772
Highly efficient therapeutic gene editing of human hematopoietic stem cells Yuxuan Wu, Jing Zeng, Benjamin P. Roscoe, Nature Medicine Induced Pluripotent Stem CellGenome SurgeryMedicineStem Cell MobilizationStem Cell Research	2019	504
Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial Maria Sessa, Laura Lorioli, Francesca Fumagalli, The Lancet Ad-hoc AnalysisCell TherapyBone Marrow FailureAutoimmune DiseaseEarly-onset Metachromatic Leukodystrophy	2016	496
Post-Transcriptional Genetic Silencing of <i>BCL11A</i> to Treat Sickle Cell Disease Erica B. Esrick, Leslie Lehmann, Alessandra Biffi, New England Journal of Medicine	2020	407
A comprehensive single cell transcriptional landscape of human hematopoietic progenitors Danilo Pellin, Mariana Loperfido, Cristina Baricordi, Nature Communications	2019	364
Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters Mario Amendola, Mary Anna Venneri, Alessandra Biffi, Nature Biotechnology Transcriptional RegulationDevelopmental BiologyEngineeringGeneticsGene Regulation	2004	325
Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells Alessandra Biffi, Michele De Palma, Angelo Quattrini, Journal of Clinical Investigation Cell TherapyImmunologyTherapeuticsGene-based DeliveryNeuroinflammation	2004	284
Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora, The Lancet	2022	266

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