Sarah Marktel

Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency

Alessandro Aiuti, Federica Cattaneo, Stefania Galimberti et al. · New England Journal of Medicine · 2009 · 1K citations · Full text

Medicine, Hematology, Immunology +16

Association of busulfan exposure with survival and toxicity after haemopoietic cell transplantation in children and young adults: a multicentre, retrospective cohort analysis

Imke H. Bartelink, Arief Lalmohamed, Elisabeth M L van Reij et al. · The Lancet Haematology · 2016 · 288 citations · Full text

Medicine, Hematology, Pediatrics +16

Hemopoietic stem cell transplantation in thalassemia: a report from the European Society for Blood and Bone Marrow Transplantation Hemoglobinopathy Registry, 2000–2010

D Baronciani, Emanuele Angelucci, Ulrike Pötschger et al. · Bone Marrow Transplantation · 2016 · 230 citations

Medicine, Hematology, Cell Therapy +11

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese et al. · Nature Medicine · 2019 · 225 citations

Medicine, Hematology, Pediatrics +14

The potential immunogenicity of the TK suicide gene does not prevent full clinical benefit associated with the use of TK-transduced donor lymphocytes in HSCT for hematologic malignancies

Catia Traversari, Sarah Marktel, Zulma Magnani et al. · Blood · 2007 · 207 citations

Medicine, Hematology, Immunology +17