Concepedia

Publication | Open Access

Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency

DOIFull Paper Access

997

Citations

30

References

2009

Year

Alessandro Aiuti, Federica Cattaneo, Stefania Galimberti, Ulrike Benninghoff, Barbara Cassani, Luciano Callegaro, Samantha Scaramuzza, Grazia Andolfi, Massimiliano Mirolo, Immacolata Brigida,
New England Journal of Medicine

Abstract

Gene therapy, combined with reduced-intensity conditioning, is a safe and effective treatment for SCID in patients with ADA deficiency. (ClinicalTrials.gov numbers, NCT00598481 and NCT00599781.)

References

YearCitations

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