Maria Rosa Lidonnici

Targeting autophagy potentiates tyrosine kinase inhibitor–induced cell death in Philadelphia chromosome–positive cells, including primary CML stem cells

Cristian Bellodi, Maria Rosa Lidonnici, Ashley Hamilton et al. · Journal of Clinical Investigation · 2009 · 561 citations · Full text

Life Sciences, Oncology, Cytogenetics +1

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese et al. · Nature Medicine · 2019 · 225 citations

Medicine, Hematology, Pediatrics +14

Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts

Arianna Moiani, Ylenia Paleari, Daniela Sartori et al. · Journal of Clinical Investigation · 2012 · 180 citations · Full text

Life Sciences, Genetics, Molecular Biology +15

Deletion of TMPRSS6 attenuates the phenotype in a mouse model of β-thalassemia

Antonella Nai, Alessia Pagani, Giacomo Mandelli et al. · Blood · 2012 · 157 citations · Full text

Medicine, Genetics, Molecular Genetics +3

Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene Therapy

Erika Zonari, Giacomo Desantis, Carolina Petrillo et al. · Stem Cell Reports · 2017 · 152 citations · Full text

Life Sciences, Cell Biology, Hematology +17