Kirsten E. Coleman

RNA aggregates harness the danger response for potent cancer immunotherapy

Héctor R. Méndez‐Gómez, Anna DeVries, Christina A. Von Roemeling et al. · Cell · 2024 · 131 citations · Full text

Life Sciences, Molecular Biology, Oncology +13

Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies

Stephanie M. Salabarria, Manuela Corti, Kirsten E. Coleman et al. · Journal of Clinical Investigation · 2023 · 128 citations · Full text

Medicine, Hematology, Nephrology +17

Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV- <i>hGAA</i> ) Gene Therapy in Children Affected by Pompe Disease

Manuela Corti, Cristina Liberati, Barbara K. Smith et al. · Human Gene Therapy Clinical Development · 2017 · 115 citations · Full text

Medicine, Hematology, Molecular Medicine +14

Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy

Sharla M. Birch, Michael W. Lawlor, Thomas J. Conlon et al. · Science Translational Medicine · 2023 · 68 citations · Full text

Medicine, Molecular Genetics, Molecular Medicine +16

A comprehensive study of a 29-capsid AAV library in a non-human primate central nervous system

Oleksandr Kondratov, Liudmyla Kondratova, Ronald J. Mandel et al. · Molecular Therapy · 2021 · 62 citations · Full text

Life Sciences, Molecular Genetics, Gene Delivery +13