Manuela Corti

Safety and Efficacy of Omaveloxolone in Friedreich Ataxia (<scp>MOXIe</scp> Study)

David R. Lynch, Melanie Chin, Martin B. Delatycki et al. · Annals of Neurology · 2020 · 296 citations · Full text

Medicine, Neurology, Pharmacology +17

B-cell depletion is protective against anti-AAV capsid immune response: a human subject case study

Manuela Corti, ME Elder, DJ Falk et al. · Molecular Therapy — Methods & Clinical Development · 2014 · 135 citations · Full text

Life Sciences, Immunology, Molecular Medicine +13

Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies

Stephanie M. Salabarria, Manuela Corti, Kirsten E. Coleman et al. · Journal of Clinical Investigation · 2023 · 128 citations · Full text

Medicine, Hematology, Nephrology +17

Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV- <i>hGAA</i> ) Gene Therapy in Children Affected by Pompe Disease

Manuela Corti, Cristina Liberati, Barbara K. Smith et al. · Human Gene Therapy Clinical Development · 2017 · 115 citations · Full text

Medicine, Hematology, Molecular Medicine +14

Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning

Manuela Corti, Brian Cleaver, Nathalie Clément et al. · Human Gene Therapy Clinical Development · 2015 · 91 citations · Full text

Medicine, Molecular Biology, Molecular Genetics +14