Thomas J. Conlon

Treatment of Leber Congenital Amaurosis Due to <i>RPE65</i> Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial

William W. Hauswirth, Tomás S. Alemán, Shalesh Kaushal et al. · Human Gene Therapy · 2008 · 937 citations · Full text

Recombinant Adeno-Associated Virus Serotype 9 Leads to Preferential Cardiac Transduction In Vivo

Christina A. Pacak, Cathryn Mah, Bijoy Thattaliyath et al. · Circulation Research · 2006 · 394 citations

Cardiac Muscle, Aav9 Gene Transfer, Vector Genomes +16

Mutational Analysis of the Adeno-Associated Virus Type 2 (AAV2) Capsid Gene and Construction of AAV2 Vectors with Altered Tropism

Pei Wu, Wu Xiao, Thomas J. Conlon et al. · Journal of Virology · 2000 · 381 citations · Full text

Human <i>RPE65</i> Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety at 1 Year

Artur V. Cideciyan, William W. Hauswirth, Tomás S. Alemán et al. · Human Gene Therapy · 2009 · 311 citations · Full text

Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy

Mark Brantly, Jeffrey D. Chulay, Lili Wang et al. · Proceedings of the National Academy of Sciences · 2009 · 311 citations · Full text

Cell Therapy, In Vivo Gene Therapy, Transgene Expression +20