Barrie J. Carter

Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

James Bainbridge, Alexander J. Smith, Susie S. Barker et al. · New England Journal of Medicine · 2008 · 1.9K citations · Full text

Gene Therapies, Ocular Disease, Retina +14

Artificial miRNAs mitigate shRNA-mediated toxicity in the brain: Implications for the therapeutic development of RNAi

Jodi L. McBride, Ryan L. Boudreau, Scott Q. Harper et al. · Proceedings of the National Academy of Sciences · 2008 · 606 citations · Full text

Knockout Mouse, Neurodegenerative Diseases, Engineering +15

Defective regulation of outwardly rectifying Cl− channels by protein kinase A corrected by insertion of CFTR

Marie E. Egan, Terence R. Flotte, Sandra Afione et al. · Nature · 1992 · 420 citations

Signal Transduction, Molecular Physiology, Signaling Pathway +13

Nonallele-specific Silencing of Mutant and Wild-type Huntingtin Demonstrates Therapeutic Efficacy in Huntington's Disease Mice

Ryan L. Boudreau, Jodi L. McBride, Inês Martins et al. · Molecular Therapy · 2009 · 334 citations · Full text

Characteristics and Taxonomy of <i>Parvoviridae</i>

G. Siegl, Robert C. Bates, Kenneth I. Berns et al. · Intervirology · 1985 · 307 citations

Infectious Disease Ecology, Emerging Infectious Diseases, Publisher.drug Dosage +12