Giulio Spinozzi

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese et al. · Nature Medicine · 2019 · 221 citations

Pediatric Hematology, Transfusion Medicine, Hematology +8

Preclinical Testing of the Safety and Tolerability of Lentiviral Vector–Mediated Above-Normal Alpha-L-Iduronidase Expression in Murine and Human Hematopoietic Cells Using Toxicology and Biodistribution Good Laboratory Practice Studies

Ilaria Visigalli, Stefania Delai, Francesca Ferro et al. · Human Gene Therapy · 2016 · 41 citations

Cell Therapy, Vector Integration Site, Immunology +16

Retrieval of vector integration sites from cell-free DNA

Daniela Cesana, Andrea Calabria, Laura Rudilosso et al. · Nature Medicine · 2021 · 40 citations · Full text

Dactinomycin induces complete remission associated with nucleolar stress response in relapsed/refractory NPM1-mutated AML

Ilaria Gionfriddo, Lorenzo Brunetti, Federica Mezzasoma et al. · Leukemia · 2021 · 38 citations · Full text

Prolonged XPO1 inhibition is essential for optimal antileukemic activity in <i>NPM1</i>-mutated AML

Giulia Pianigiani, Andrea Gagliardi, Federica Mezzasoma et al. · Blood Advances · 2022 · 36 citations · Full text

Hematological Malignancy, Mutant Npm1, Prolonged Xpo1 Inhibition +13