Virginie François

Misregulated alternative splicing of BIN1 is associated with T tubule alterations and muscle weakness in myotonic dystrophy

Charlotte Fugier, Arnaud F. Klein, Caroline Hammer et al. · Nature Medicine · 2011 · 325 citations

T Tubule Alterations, Medicine, Genetics +6

Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

Caroline Le Guiner, Laurent Servais, Marie Montus et al. · Nature Communications · 2017 · 230 citations · Full text

Characterization of Dystrophin Deficient Rats: A New Model for Duchenne Muscular Dystrophy

Thibaut Larcher, Aude Lafoux, Laurent Tesson et al. · PLoS ONE · 2014 · 182 citations · Full text

Muscle Function, Pathology, Rat Model +17

Forelimb Treatment in a Large Cohort of Dystrophic Dogs Supports Delivery of a Recombinant AAV for Exon Skipping in Duchenne Patients

Caroline Le Guiner, Marie Montus, Laurent Servais et al. · Molecular Therapy · 2014 · 114 citations · Full text

Selective silencing of mutated mRNAs in DM1 by using modified hU7-snRNAs

Virginie François, Arnaud F. Klein, Cyriaque Beley et al. · Nature Structural & Molecular Biology · 2010 · 75 citations · Full text

Natural Sciences, Genetics, Rna Biology +7