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Exagamglogene Autotemcel for Severe Sickle Cell Disease

304

Citations

13

References

2024

Year

Abstract

Treatment with exa-cel eliminated vaso-occlusive crises in 97% of patients with sickle cell disease for a period of 12 months or more. (CLIMB SCD-121; ClinicalTrials.gov number, NCT03745287.).

References

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