Concepedia

Ami J. Shah

AJ

48

Publications

3.4K

Citations

30

H-Index

1994

Active since

Affiliations

Children's Hospital of Los Angeles(Current)

University of California, Los Angeles

Medical College of Wisconsin

National Institutes of Health

Fred Hutch Cancer Center

Ami J. Shah is an author at Children's Hospital of Los Angeles specializing in medicine, hematology, and transplantation.

ORCID

Top concepts

Publications per year

1994–2024

48

Publications

48

Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy

Florian Eichler, Christine Duncan, Patricia L. Musolino et al. · New England Journal of Medicine · 2017 · 575 citations · Full text

Exagamglogene Autotemcel for Severe Sickle Cell Disease

Haydar Frangoul, Franco Locatelli, Akshay Sharma et al. · New England Journal of Medicine · 2024 · 304 citations

Adenoviral infections and a prospective trial of cidofovir in pediatric hematopoietic stem cell transplantation

Jill A. Hoffman, Ami J. Shah, Lawrence A. Ross et al. · Biology of Blood and Marrow Transplantation · 2001 · 237 citations · Full text

Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans

Fabio Candotti, Kit L. Shaw, Linda Muul et al. · Blood · 2012 · 233 citations · Full text

Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency

Donald B. Kohn, Claire Booth, Kit L. Shaw et al. · New England Journal of Medicine · 2021 · 205 citations · Full text

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