Maria Domenica Cappellini

CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

Haydar Frangoul, David Altshuler, Maria Domenica Cappellini et al. · New England Journal of Medicine · 2020 · 1.9K citations · Full text

Life Sciences, Genetics, Hematology +17

Survival and complications in patients with thalassemia major treated with transfusion and deferoxamine.

Caterina Borgna‐Pignatti, Simone Rugolotto, Piero De Stefano et al. · PubMed · 2004 · 1.1K citations

Medicine, Cardiology, Hematology +15

A phase 3 study of deferasirox (ICL670), a once-daily oral iron chelator, in patients with beta-thalassemia

Maria Domenica Cappellini · Blood · 2005 · 719 citations · Full text

Medicine, Hematology, Pharmacology +13

Guidelines for the Management of Transfusion Dependent Thalassaemia (TDT)

Maria Domenica Cappellini, Alan R. Cohen, John B. Porter et al. · 2014 · 403 citations

Medicine, Hematology, Internal Medicine +10

Hematopoietic stem cell transplantation in thalassemia major and sickle cell disease: indications and management recommendations from an international expert panel

Emanuele Angelucci, Susanne Matthes‐Martin, D Baronciani et al. · Haematologica · 2014 · 382 citations · Full text

Medicine, Hematology, Cell Therapy +16