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Safety and efficacy of nusinersen in spinal muscular atrophy: The <scp>EMBRACE</scp> study

DOIFull Paper Access

107

Citations

21

References

2021

Year

Gyula Acsádi, Thomas O. Crawford, Wolfgang Müller‐Felber, Perry B. Shieh, Randal Richardson, Niranjana Natarajan, Diana Castro, Daniela Ramirez‐Schrempp, Giulia Gambino, Peng Sun,
Muscle & Nerve

Abstract

Nusinersen demonstrated a favorable long-term benefit-risk profile in this broad population of individuals with infantile- or later-onset SMA.

References

YearCitations

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