Direct Gene Transfer into Mouse Muscle in Vivo

Jon A. Wolff, Robert W. Malone, Phillip Williams, +4

Science

Long-term persistence of plasmid DNA and foreign gone expression in mouse muscle

Jon A. Wolff, James J. Ludtke, Gyula Acsádi, +2

Human Molecular Genetics

Muscle FunctionGeneticsMolecular BiologyGene CharacterizationMolecular Genetics +20

Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs

Gyula Acsádi, George Dickson, Donald R. Love, +5

Nature

Mdx MiceDna ConstructsImmunologyIntramuscular InjectionDegenerative Disease +3

The route of administration is a major determinant of the transduction efficiency of rat tissues by adenoviral recombinants.

Johnny Huard, Hanns Lochmüller, Gyula Acsádi, +3

PubMed

Conditions affecting direct gene transfer into rodent muscle in vivo.

Wolff Ja, Priscilla A. Williams, Gyula Acsádi, +2

PubMed

MechanobiologyMuscle PhysiologyMuscle CellsXenotransplantationHealth Sciences +13

Direct gene transfer and expression into rat heart in vivo.

Gyula Acsádi, S Jiao, A Jani, +3

PubMed

Cardiac MuscleCardiomyopathyDna UptakeCardiac ReprogrammingIn Vivo Gene Therapy +13

A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity

Gyula Acsádi, Ágnes Jáni, Bernard Massie, +4

Human Molecular Genetics

Skeletal Muscle CellsViral ReplicationDifferential EfficiencyImmunologyCellular Physiology +16

Emergence of Early Region 1-Containing Replication-Competent Adenovirus in Stocks of Replication-Defective Adenovirus Recombinants (ΔE1 + ΔE3) During Multiple Passages in 293 Cells

Hanns Lochmüller, A Jani, Johnny Huard, +5

Human Gene Therapy

Gene Transfer into Skeletal Muscles by Isogenic Myoblasts

Johnny Huard, Gyula Acsádi, Ágnes Jáni, +2

Human Gene Therapy

Mutations in BICD2 Cause Dominant Congenital Spinal Muscular Atrophy and Hereditary Spastic Paraplegia

Emily C. Oates, Alexander M. Rossor, Majid Hafezparast, +23

The American Journal of Human Genetics

Rare DiseasesMendelian DisorderGenetic DisorderMedicineGenetics +6