Publication | Closed Access
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study
998
Citations
28
References
2016
Year
Dose-escalation StudySpinal Cord InjuryPediatric SpinePhase 2Neuromusculoskeletal DisorderMedicineSpinal DisorderOrthopaedic SurgeryNeuromuscular Pathology
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