Nature Cell Biology · 2020 · 40 citations · 42 references
Life SciencesGeneticsImmunologyImmunoregulationImmunotherapyInnate ImmunityCrispr-based EngineeringCrispr-cas SystemsTherapeutic Genome EditingCrispr-based Genome EngineeringCrispr-cas Genome EditingCrispr-cas RegulationIn Vivo Genome EditingTherapeutic Immunomodulation
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CRISPR-Mediated Modular RNA-Guided Regulation of Transcription in Eukaryotes
Luke A. Gilbert, Matthew H. Larson, Leonardo Morsut et al. · Cell · 2013 · 3.8K citations · Full text
Mutations in PCSK9 cause autosomal dominant hypercholesterolemia
Marianne Abifadel, Mathilde Varret, Jean‐Pierre Rabès et al. · Nature Genetics · 2003 · 3K citations
Genome-scale transcriptional activation by an engineered CRISPR-Cas9 complex
Silvana Konermann, Mark D. Brigham, Alexandro E. Trevino et al. · Nature · 2014 · 2.9K citations
Genome-Scale CRISPR-Mediated Control of Gene Repression and Activation
Luke A. Gilbert, Max A. Horlbeck, Britt Adamson et al. · Cell · 2014 · 2.9K citations · Full text
Toll-like receptors control activation of adaptive immune responses
Markus Schnare, Gregory M. Barton, Agnieszka Czopik Holt et al. · Nature Immunology · 2001 · 1.4K citations