Concepedia

Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing

José Bonafont, Ángeles Mencía, Marta García, Raúl Torres, Sandra Rodríguez, Marta Carretero, Esteban Chacón-Solano, Silvia Modamio‐Høybjør, Lucía Marinas, Carlos León,

Molecular Therapy · 2019 · 108 citations · 29 references

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References

29

Highly efficient RNA-guided genome editing in human cells via delivery of purified Cas9 ribonucleoproteins

Sojung Kim, Daesik Kim, Seung Woo Cho et al. · Genome Research · 2014 · 1.9K citations · Full text

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p63 identifies keratinocyte stem cells

Graziella Pellegrini, Elena Dellambra, Osvaldo Golisano et al. · Proceedings of the National Academy of Sciences · 2001 · 1.4K citations · Full text

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Identification of preexisting adaptive immunity to Cas9 proteins in humans

Carsten T. Charlesworth, Priyanka S. Deshpande, Daniel P. Dever et al. · Nature Medicine · 2019 · 975 citations · Full text

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CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells

Daniel P. Dever, Rasmus O. Bak, Andreas Reinisch et al. · Nature · 2016 · 876 citations · Full text

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Rapid and highly efficient mammalian cell engineering via Cas9 protein transfection

Xiquan Liang, Jason Potter, Shantanu Kumar et al. · Journal of Biotechnology · 2015 · 753 citations · Full text

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