Disulfide-functional poly(amido amine)s with tunable degradability for gene delivery

A versatile vector for gene and oligonucleotide transfer into cells in culture and in vivo: polyethylenimine.

Otmane Boussif, Frank Lezoualc’h, Maria Antonietta Zanta et al. · Proceedings of the National Academy of Sciences · 1995 · 6.2K citations · Full text

Engineering, In Vivo Gene Therapy, Several Polycations +20

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

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Inflammation, Aav-factor Ix, Host Response +11

Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells.

Jane C. Burns, T Friedmann, Wolfgang Driever et al. · Proceedings of the National Academy of Sciences · 1993 · 1.4K citations · Full text

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

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Cell Therapy, Immunology, Blood Cell +17

Tumor Regression by Targeted Gene Delivery to the Neovasculature

John Hood, Mark D. Bednarski, Ricardo F. Frausto et al. · Science · 2002 · 858 citations