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Elimination of lysosomal storage in brains of MPS VII mice treated by intrathecal administration of an adeno-associated virus vector

Mps Vii MiceViral ReplicationMolecular VirologyNeurovirologyLysosomal StorageIntrathecal AdministrationViral PathogenesisMedicineVirologyNeuroscienceNeuroimmunologyCell BiologyLysosomal Storage Disease